At Safi Biotherapeutics, we manufacture adult stem-cell derived, human red blood cells (mRBCs), with the goal of providing a highly characterized cell therapy blood transfusion product at industrial scale and viable economics for civilian and military transfusion needs. Blood is the most prescribed biologic therapy in the world. Blood donor supply shortages continue to be a global crisis, and we are uniquely positioned to provide a safe and reliable blood supply to meet this challenge. Our mRBCs have valuable potential use in chronic transfusion indications as well as in acute transfusion settings, such as hospitals and battlefields.
Safi’s manufacturing blueprint for red blood cell production is the most advanced in the industry. Our collaboration with ARMI | BioFabUSA, a non-profit organization and U.S. Department of War Manufacturing Innovation Institute, is supporting the GMP production of mRBCs for clinical trials. This collaboration, alongside our proprietary advanced biomanufacturing processes, enables the manufacture of units of ultra-high densities of mRBCs in 10-liter scale bioreactors that consistently meet strict purity and quality standards. GMP manufacturing for initial clinical studies at 10-liter scale is currently underway.
We continue to advance our research of cryopreserved and freeze-dried mRBCs, which present innovative solutions across civilian and military settings, particularly with respect to pre-hospital use and government stockpiling. We have achieved proof of principle showing our mRBCs are more resistant to the detrimental effects of both cryopreservation (without glycerol) and freeze-drying. This early work provides a foundation for optimization of cell specification and formulation that maximizes product viability for long-term storage and transport.
Founded in 2020 as the cell therapy commercialization partner of the U.S. Defense Health Agency On-Demand Blood program, Safi has received more than $20 million in non-dilutive government funding and completed a $5 million private seed investment. These investments are accelerating the GMP manufacturing of our red blood cells at clinically meaningful scale and the completion of IND-enabling activities for clinical trial initiation in 2027. In 2024, the U.S. Food and Drug Administration granted our mRBCs Rare Pediatric Disease Designation and Orphan Drug Designation for use in the chronic transfusion of patients with sickle cell disease.
Safi Biotherapeutics leadership comprises industry and cell therapy veterans from the Defense Advanced Research Projects Agency (DARPA), Vertex Pharmaceuticals, Mass General Brigham and Loughborough University in the United Kingdom. They bring experience in ex vivo human blood cell development, biologic and pharmaceutical manufacturing, pre-clinical and clinical development, and regulatory submissions.